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NCT03775174 Clinical Trial

Expanded Access to Mepsevii

Mucopolysaccharidosis VII Clinical Trial

Clinical Trial Details — Status: Available

Administrative data
NCT number NCT03775174
Other study ID # UX003-EAP
Secondary ID
Status Available
Phase
First received
Last updated

Study information
Verified date June 2024
Source Ultragenyx Pharmaceutical Inc
Contact Early Access
Phone 1-415-483-8800
Email EarlyAccess@ultragenyx.com
Is FDA regulated No
Health authority
Study type Expanded Access

Clinical Trial Summary

Individual patient expanded access requests may be considered for patients who have no other treatment options

Description:

Expanded access may be available outside of the US in countries prior to approval by the local regulatory agencies. For full details, please visit the links provided below.

Recruitment information / eligibility
Status Available
Enrollment 0
Est. completion date
Est. primary completion date
Accepts healthy volunteers
Gender All
Age group N/A and older
Eligibility Inclusion Criteria: - Exclusion Criteria: -

Study Design

Related Conditions & MeSH terms

Intervention

Drug:
• Mepsevii

Locations
Country Name City State
n/a

Sponsors (1)
Lead Sponsor Collaborator
Ultragenyx Pharmaceutical Inc
See also
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Recruiting NCT05619900 - Registry of Patients Diagnosed With Lysosomal Storage Diseases
Enrolling by invitation NCT05368038 - ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
Completed NCT02418455 - Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Treatment in Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7) Patients Less Than 5 Years of Age Phase 2
Recruiting NCT03604835 - Mucopolysaccharidosis VII Disease Monitoring Program
Recruiting NCT06036693 - MPS (RaDiCo Cohort) (RaDiCo-MPS)

External Links