Study of rhASB in Patients With Mucopolysaccharidosis VI

Status Completed

Clinical Trial Summary

The purpose of this study is to evaluate the long-term efficacy and safety of rhASB treatment in patients with Mucopolysaccharidosis VI.

Clinical Trial Description

n/a

Study Design

Allocation: Non-Randomized, Endpoint Classification: Safety/Efficacy Study, Intervention Model: Single Group Assignment, Masking: Open Label, Primary Purpose: Treatment

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT00104234
Study type	Interventional
Source	BioMarin Pharmaceutical
Contact
Status	Completed
Phase	Phase 3
Start date	February 2004
Completion date	October 2006

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See also
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