Mucopolysaccharidosis II Clinical Trial
Official title:
Immunophenotyping of Patients With MPS II Treated With Enzyme Replacement Therapy
The purpose of this study is to investigate how participant's body's immune system responds to idursulfase, an enzyme replacement therapy (ERT) and find out which types of immune cells are involved in causing untoward responses to the ERT so that the investigators can relate the level of immune response to the treatment.
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| Status | Clinical Trial | Phase | |
|---|---|---|---|
| Withdrawn |
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