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Long Term Follow-up (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX — LTFU  

Hemophilia B Clinical Trial

Official title:
Long-Term Follow-up of Subjects Who Were Treated With SB-318, SB-913, or SB-FIX, for Targeted Genome Editing Into the Albumin Gene in the Liver

Clinical Trial Summary

Long-term follow-up of subjects who received SB-318, SB-913, or SB-FIX in a previous trial and completed at least 52 weeks post-infusion follow-up in their primary protocol. Enrolled subjects will be followed for a total of up to 10 years following exposure to SB-318, SB-913, or SB-FIX.

Clinical Trial Description

Non-interventional, multi-center, long-term follow-up (LTFU) study of subjects dosed with SB-318 in the clinical study SB-318-1502, SB-913 in the clinical study SB-913-1602, and SB-FIX in clinical study SB-FIX-1501. All subjects dosed in the studies and completed at least 52 weeks post-infusion follow-up in their primary protocol will be offered to participate. Subjects who enroll will be monitored for a total of up to 10 years following exposure to the respective investigational products. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04628871
Study type Observational
Source Sangamo Therapeutics
Contact
Status Active, not recruiting
Phase
Start date November 3, 2020
Completion date January 1, 2030
View Details
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