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An Extension Study of JR-141 in Patients With Mucopolysaccharidosis Type II

Mucopolysaccharidosis II Clinical Trial

Official title:
An Extension Study of JR-141 in Patients With Mucopolysaccharidosis Type II

Clinical Trial Summary

Multicenter, open-label, single-group, designed to evaluate the long term efficacy and safety of study drug for the treatment of the MPS II.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04348136
Study type Interventional
Source JCR Pharmaceuticals Co., Ltd.
Contact
Status Active, not recruiting
Phase Phase 2/Phase 3
Start date September 1, 2019
Completion date March 31, 2030
View Details
See also
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