A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle

Updated 06/21/2024

Status Terminated

Clinical Trial Summary

This study is designed to evaluate the safety and efficacy of deflazacort in participants with LGMD2I. Most participants enrolled will have a screening visit and 3 additional visits (after 1, 13, and 26 weeks of treatment).

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT03783923
Study type	Interventional
Source	PTC Therapeutics
Contact
Status	Terminated
Phase	Phase 3
Start date	October 31, 2019
Completion date	January 1, 2021

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