An Observational Study of Pediatric Subjects With Globoid Cell Leukodystrophy (GLD)

Leukodystrophy, Globoid Cell Clinical Trial

Official title:
A Multicenter, Prospective, Longitudinal, Observational Study of Pediatric Subjects With Globoid Cell Leukodystrophy (Krabbe Disease)

Status Withdrawn

Clinical Trial Summary

The objective of this study is to evaluate the natural history of disease progression in infants with globoid cell leukodystrophy (GLD).

Clinical Trial Description

This study is being conducted to gather prospective data on disease progression in infants diagnosed with GLD. This study will be performed using protocol-defined, standardized assessments including clinical, developmental, and neurologic measures. All study visits will be conducted in the subject's home. No travel to the study site is necessary. ;

Study Design

Related Conditions & MeSH terms

Leukodystrophy, Globoid Cell

Clinical Trial Details

NCT number	NCT01093105
Study type	Observational
Source	Takeda
Contact
Status	Withdrawn
Phase
Start date	April 1, 2010
Completion date	May 1, 2012

View Details

See also
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Completed	`NCT00006057` - Diagnostic and Screening Study of Genetic Disorders	N/A