Infantile Neuroaxonal Dystrophy Clinical Trial
Official title:
A Retrospective Review of the Natural History of Infantile Neuroaxonal Dystrophy
This is a retrospective and cross-sectional review of the natural history of INAD.
After obtaining informed consent, the study participants' relevant medical records will be collected and reviewed. If needed, a telephone or video conference will be scheduled with the patient's family to confirm and clarify information in the medical record. Deceased patients may be eligible for inclusion the retrospective registry if medical records are sufficient and indicate eligibility. Data will be pooled and presented in aggregate, without identification of individual subjects. ;
| Status | Clinical Trial | Phase | |
|---|---|---|---|
| Active, not recruiting |
NCT03570931 -
A Study to Assess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal Dystrophy
|
Phase 2/Phase 3 | |
| Terminated |
NCT03726996 -
Desipramine in Infantile Neuroaxonal Dystrophy (INAD).
|
Phase 4 |