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Clinical Trial Summary

This is a multi-center, single-arm, open-label, single-dose treatment clinical study to evaluate the safety, tolerability and efficacy of BBM-H901 injection in Hemophilia B subjects with ≤2 International unit per deciliter (IU/dl) residual factor IX (FIX) levels. BBM-H901 is an adeno-associated virus (AAV) vector derived from recombinant DNA techniques to contain an expression cassette of the human factor IX (hFIX) transgene and raises circulating levels of endogenous FIX.

Clinical Trial Description


Study Design

Related Conditions & MeSH terms

NCT number NCT05203679
Study type Interventional
Source Shanghai Belief-Delivery BioMed Co., Ltd
Contact Li Chen, Master
Phone 16602669908
Status Recruiting
Phase Phase 1/Phase 2
Start date December 30, 2021
Completion date June 30, 2028

See also
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