Non-Interventional Study to Capture the Patient Experience on Gene Therapy

See also
Status	Clinical Trial	Phase
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Completed	`NCT02199717` - An Institutional Pilot Study to Investigate Physical Activity Patterns in Boys With Hemophilia	N/A
Completed	`NCT01662531` - A Safety, Efficacy and Pharmacokinetics Study of a Recombinant Fusion Protein Linking Coagulation Factor IX With Albumin (rIX-FP) in Children With Hemophilia B	Phase 3
Completed	`NCT01335061` - Study To Compare On-Demand Treatment To A Prophylaxis Regimen Of BeneFIX In Subjects With Moderately Severe to Severe Hemophilia B	Phase 3
Completed	`NCT01217255` - Comparing the Burden of Illness of Hemophilia in the Developing and the Developed World
Completed	`NCT00037557` - Study Evaluating rFIX; BeneFIX in Severe Hemophilia B	Phase 3
Completed	`NCT02554773` - An Open-label Extension Study of an Investigational Drug, Fitusiran, in Patients With Moderate or Severe Hemophilia A or B	Phase 1/Phase 2
Terminated	`NCT02807753` - The Hemophilia Ultrasound Project
Active, not recruiting	`NCT03901755` - An International Study to Evaluate the Real-world Effectiveness and Usage of Alprolix in Patients With Haemophilia B
Not yet recruiting	`NCT05980377` - Patterns of Hemophilia Care in Assiut Children Patients
Recruiting	`NCT05687474` - Baby Detect : Genomic Newborn Screening
Terminated	`NCT03248141` - Understanding Hemophilia A and B Drug Dosage Administration Patterns
Terminated	`NCT01460147` - Osteoporosis and MRI Study in Hemophilia	N/A
Completed	`NCT03818529` - ATHN 8: Previously Untreated Patients (PUPs) Matter Study
Completed	`NCT02571569` - A Single Escalating Dose and Multiple Dose Study of BAY 1093884 in Subjects With Severe Hemophilia Types A or B, With or Without Inhibitors	Phase 1
Terminated	`NCT01620801` - Hemophilia B Gene Therapy With AAV8 Vector	Phase 1
Completed	`NCT01233440` - Safety and Pharmacokinetic Study of a Recombinant Coagulation Factor IX Albumin Fusion Protein in Subjects With Hemophilia B	Phase 1
Active, not recruiting	`NCT04135300` - Gene Therapy for Chinese Hemophilia B	N/A
Enrolling by invitation	`NCT03655223` - Early Check: Expanded Screening in Newborns
Terminated	`NCT00947193` - Study of Ataluren (PTC124) in Hemophilia A and B	Phase 2

NCT number	NCT03054389
Study type	Observational
Source	Takeda
Contact
Status	Completed
Phase
Start date	March 31, 2017
Completion date	June 6, 2017

Non-Interventional Study to Capture the Patient Experience on Gene Therapy for Hemophilia Within the AskBio009-101 Study Through Patient and Investigator Interviews

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms