An Expanded Access Program of Emicizumab in Participants With Hemophilia A

Clinical Trial Summary

This open-label, multicenter expanded access program (EAP) is designed to provide emicizumab to eligible participants with hemophilia A with factor VIII (FVIII) inhibitors before it is commercially available in the United States for the indication of hemophilia A with FVIII inhibitors. Discontinuation may occur earlier if participant or physician decides to discontinue treatment or the sponsor discontinues emicizumab clinical development.

See also
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NCT number	NCT03154437
Study type	Expanded Access
Source	Genentech, Inc.
Contact
Status	Approved for marketing
Phase

An Expanded Access Program of Emicizumab in Participants With Hemophilia A With Inhibitors

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms