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Clinical Trial Summary

This Phase I/II clinical study will evaluate the safety and efficacy of valoctocogene roxaparvovec in patients with severe haemophilia A and inhibitors to FVIII. Part A of the study will involve subjects who have active inhibitors to FVIII, and Part B involving subjects with a prior history of inhibitors.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT04684940
Study type Interventional
Source BioMarin Pharmaceutical
Contact Trial Specialist
Phone 1-800-983-4587
Email medinfo@bmrn.com
Status Recruiting
Phase Phase 1/Phase 2
Start date December 10, 2020
Completion date February 2029

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