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Haemoglobinopathies clinical trials

View clinical trials related to Haemoglobinopathies.

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NCT ID: NCT04746066 Recruiting - Haemoglobinopathies Clinical Trials

Observational Study for Patients With Hemoglobinopathies and Rare Inherited Anemia and Covid 19

Start date: March 31, 2020
Phase:
Study type: Observational

The COVID-19 pandemic is causing many deaths around the world, putting a strain on health services. Patients with pre-existing chronic conditions are most affected by the SARS-COV2 infection. Infectious complications are a common cause of mortality and one of the main causes of morbidity in all these diseases. The main objective of this project is the assessment of patients with thalassemia, drepanocytosis, other haemoglobinopathies and rares inherited anemias suffering from SARS-COV-2 to: 1. Obtain clinical and epidemiological data that can provide information on a possible increased vulnerability of these patients to SARS-COV-2 infection; 2. Sharing therapeutic approaches considering the lack of information about the treatment.

NCT ID: NCT02349906 Completed - Clinical trials for Inborn Errors of Metabolism

Treosulfan-based Versus Busulfan-based Conditioning in Paediatric Patients With Non-malignant Diseases

Start date: April 2015
Phase: Phase 2
Study type: Interventional

The aim of the trial is to describe the safety and efficacy of intravenous (i.v.) Treosulfan compared to the conventional (myeloablative) dose of i.v. Busulfan, each administered as part of a standardised Fludarabine-containing conditioning regimen and to contribute to a PK model which permits - in conjunction with data comparing Treosulfan and Busulfan in adults with malignant diseases - to extend the use of Treosulfan in the paediatric population by extrapolating efficacy.