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Intra-Erythrocyte Dexamethasone Sodium Phosphate in Ataxia Teleangiectasia Patients — IEDAT01  

Genetic Syndrome Clinical Trial

Official title:
Evaluations of Effects of Intra-Erythrocyte Dexamethasone Sodium Phosphate on Neurological Symptoms in Ataxia Teleangiectasia Patients

Clinical Trial Summary

Multi-centre, single arm, open label, 6 months, phase II study to evaluate the effect of Ery-Dex in improving Central Nervous System (CNS) symptoms in patients with Ataxia Teleangiectasia (AT). The study consists of a screening period (max duration of 30 days) and a treatment period (duration 6 months).

Clinical Trial Description

The study has the aim to evaluate the improvement in CNS symptoms measured by International Co-operative Ataxia Rating Scale (ICARS) in patients with AT, during a period of treatment with Ery-Dex (dexamethasone sodium phosphate ex vivo encapsulated into human autologous erythrocytes). ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT01255358
Study type Interventional
Source Erydel
Contact
Status Completed
Phase Phase 2
Start date February 2011
Completion date December 2011
View Details
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