Phase 1 Study of ELX-02 in Healthy Adult Subjects

Status Completed

Clinical Trial Summary

Phase 1 Multiple Ascending Dose Study in Normal Healthy Volunteers

Clinical Trial Description

This is a study in humans of ELX-02, an advanced synthetic aminoglycoside optimized as a translational read-through drug (TRID) for the treatment of genetic conditions caused by nonsense mutations. This is a classical Phase 1b study designed as a randomized, double-blinded, placebo-controlled, multiple dose escalation to evaluate the safety, tolerability, and pharmacokinetics of ELX-02 in healthy adult volunteers. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT03309605
Study type	Interventional
Source	Eloxx Pharmaceuticals, Inc.
Contact
Status	Completed
Phase	Phase 1
Start date	October 11, 2017
Completion date	July 17, 2019

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