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A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia

Friedreich Ataxia Clinical Trial

Official title:
Long-Term Open-Label Study to Assess the Safety and Efficacy of Vatiquinone in Patients With Friedreich Ataxia

Clinical Trial Summary

The primary objective of this study is to assess the long-term safety of vatiquinone in participants with Friedreich ataxia (FA) previously exposed to vatiquinone.

Clinical Trial Description

This long-term, open-label study will serve as a continued access study for participants with FA who have previously participated in a vatiquinone study. The purpose of this study is to assess continued safety and efficacy of vatiquinone dosing in previously treated participants. This study addresses the medical need for participants to continue vatiquinone with a planned study duration of 3 years. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT05515536
Study type Interventional
Source PTC Therapeutics
Contact
Status Enrolling by invitation
Phase Phase 3
Start date December 8, 2022
Completion date December 31, 2027
View Details
See also
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