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Clinical Trial Summary

The primary objective of the study is to assess the pharmacokinetics (PK) and safety of vatiquinone administered in participants with Friedreich ataxia (FA) younger than 7 years.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT05485987
Study type Interventional
Source PTC Therapeutics
Contact
Status Active, not recruiting
Phase Phase 2
Start date October 13, 2022
Completion date October 5, 2024

See also
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