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A Study of Replagal in Treatment-naïve Adults With Fabry Disease

Fabry Disease Clinical Trial

Official title:
A Phase 3, Open-label Study to Evaluate the Efficacy and Safety of REPLAGAL® in Treatment-naïve Subjects With Fabry Disease

Clinical Trial Summary

In this study, adults with Fabry Disease who have not had any treatment for this condition will be treated with Replagal. The main aim of the study is to check if Replagal improves kidney function and heart structure of participants with Fabry Disease. Participants will receive one Replagal infusion every other week for up to 104 weeks. They will visit the clinic every 12 to 14 weeks during treatment with a follow-up visit 2 weeks after treatment.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04840667
Study type Interventional
Source Takeda
Contact
Status Terminated
Phase Phase 3
Start date December 28, 2021
Completion date December 16, 2022
View Details
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