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Clinical Trial Summary

This is a prospective multicenter, open-label, dose-escalation trial to assess the safety, tolerability, and pharmacodynamics of 4D-310 following a single IV administration. The study population is comprised of adult males and females with Fabry Disease.


Clinical Trial Description

This is a prospective multicenter, open-label, dose-escalation trial to assess the safety, tolerability, and pharmacodynamics of 4D-310 following a single IV administration. The study population is comprised of adult males and females with Fabry Disease. ;


Study Design


Related Conditions & MeSH terms


NCT number NCT04519749
Study type Interventional
Source 4D Molecular Therapeutics
Contact
Status Active, not recruiting
Phase Phase 1/Phase 2
Start date September 1, 2020
Completion date June 2027

See also
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