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Clinical Trial Summary

This study evaluates predictors for the incidence of arrhythmias and sudden cardiac death as well as terminal heart failure in patients with Fabry disease.


Clinical Trial Description

Fabry disease is a rare disease and part of the group of lysosomal storage disorders. Natural history of Fabry disease has proven poor survival to ages >50 years outlining the importance to evaluate cardiac symptoms and outcomes of patients with Fabry disease. This study is a prospective cohort study and observes patients since 2001. Through this long-term experience and the relative high number of patients this study is suggested to help estimating the risk of cardiac arrhythmias and sudden cardiac death (SCD) as well as death or heart transplantation due to terminal heart failure. All patients in treatment in the Fabry Center Wuerzburg (FAZiT) are included in this study if informed consent is provided. ;


Study Design


Related Conditions & MeSH terms


NCT number NCT03362164
Study type Observational
Source Wuerzburg University Hospital
Contact Peter Nordbeck, MD, PhD
Phone 004993120139181
Email nordbeck_p@ukw.de
Status Recruiting
Phase
Start date January 2001
Completion date March 2032

See also
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