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Clinical Trial Summary

The study will evaluate the safety and efficacy of delandistrogene moxeparvovec gene transfer therapy in non-ambulatory and ambulatory males with DMD. This is a randomized, double-blind, placebo-controlled 2-part study. Participants will be in the study for approximately 128 weeks. All participants will have the opportunity to receive intravenous (IV) delandistrogene moxeparvovec in either Part 1 or Part 2.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT05881408
Study type Interventional
Source Sarepta Therapeutics, Inc.
Contact Sarepta Therapeutics Inc., For Clinical Trial Information, Selec
Phone 1-888-SAREPTA (1-888-727-3782)
Email SareptAlly@sarepta.com
Status Recruiting
Phase Phase 3
Start date May 31, 2023
Completion date January 31, 2027

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