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Clinical Trial Summary

This is an observational screening study to evaluate the prevalence of anti-adeno-associated serotype 8 (AAV8) antibodies in participants with Duchenne muscular dystrophy (DMD).


Clinical Trial Description

This is an observational screening study to evaluate the prevalence of anti-adeno-associated serotype 8 (AAV8) antibodies in participants with Duchenne muscular dystrophy (DMD). Information collected in this study may be used to identify potential participants for DMD investigational gene therapy clinical trials. This study consists of: - A phone/video interview to provide e-consent and medical history - A single home health visit to collect blood sample for antibody testing - A phone/video call for communication of AAV8 antibody test results ;


Study Design


Related Conditions & MeSH terms


NCT number NCT05683379
Study type Observational
Source REGENXBIO Inc.
Contact Patient Advocacy
Phone 866-860-0117
Email Duchenne@regenxbio.com
Status Recruiting
Phase
Start date December 20, 2022
Completion date December 2024

See also
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