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Clinical Trial Summary

Current methods of measuring the response to new treatments for muscular dystrophies involve the examination of small pieces of muscle tissue called biopsies. The investigators are interested in finding less invasive methods that reduce the need for muscle biopsies. The purpose of this research is to learn about the possibility of detecting and measuring the activity and severity of muscular dystrophies by examining a urine sample and a blood sample.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT05016908
Study type Observational
Source Massachusetts General Hospital
Contact Tamkin Shahraki, MD
Phone 617-726-7506
Email tshahraki@mgh.harvard.edu
Status Recruiting
Phase
Start date November 30, 2019
Completion date May 2024

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