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Clinical Trial Summary

Dystrophinopathy is a term of X-linked recessive genetic disease, including Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and the X-linked dilated cardiomyopathy. The aim of this study is to determine the clinical spectrum and natural progression of dystrophinopathy in a prospective multicenter natural history study, to assess the clinical, genetic of patients with dystrophinopathy to optimize clinical management.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT04012671
Study type Observational
Source First Affiliated Hospital of Fujian Medical University
Contact Ning Wang, MD, PhD
Phone 13805015340
Email ningwang@fjmu.edu.cn
Status Recruiting
Phase
Start date July 1, 2019
Completion date December 31, 2049

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