A Registered Cohort Study on Duchenne Muscular Dystrophy

Status Recruiting

Clinical Trial Summary

Dystrophinopathy is a term of X-linked recessive genetic disease, including Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and the X-linked dilated cardiomyopathy. The aim of this study is to determine the clinical spectrum and natural progression of dystrophinopathy in a prospective multicenter natural history study, to assess the clinical, genetic of patients with dystrophinopathy to optimize clinical management.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT04012671
Study type	Observational
Source	First Affiliated Hospital of Fujian Medical University
Contact	Ning Wang, MD, PhD
Phone	13805015340
Email	ningwang@fjmu.edu.cn
Status	Recruiting
Phase
Start date	July 1, 2019
Completion date	December 31, 2049

View Details

See also
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