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Clinical Trial Details — Status: Completed

Administrative data

NCT number NCT00004312
Other study ID # NCRR-M01RR00827-1196
Secondary ID UCSD-970026UCSD-
Status Completed
Phase N/A
First received October 18, 1999
Last updated June 23, 2005
Start date October 1999

Study information

Verified date December 2003
Source National Center for Research Resources (NCRR)
Contact n/a
Is FDA regulated No
Health authority United States: Federal Government
Study type Observational

Clinical Trial Summary

OBJECTIVES: I. Establish a computerized databank to monitor the progress of patients with cystinosis treated with cysteamine.

II. Track and monitor all patients including renal transplant, dialysis and post renal transplants.


Description:

PROTOCOL OUTLINE:

Data are collected from patients and physicians. Information includes disease, treatment, family history, demographic, and physical exam data. The dates of kidney transplantation and/or dialysis initiation are also recorded.


Recruitment information / eligibility

Status Completed
Enrollment 400
Est. completion date
Est. primary completion date
Accepts healthy volunteers No
Gender Both
Age group N/A and older
Eligibility PROTOCOL ENTRY CRITERIA:

Nephropathic cystinosis diagnosis by white-cell cystine measurement, including infantile and late-onset forms

Study Design

Primary Purpose: Screening


Related Conditions & MeSH terms


Locations

Country Name City State
United States University of California San Diego School of Medicine La Jolla California

Sponsors (3)

Lead Sponsor Collaborator
National Center for Research Resources (NCRR) Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD), University of California, San Diego

Country where clinical trial is conducted

United States, 

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