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A Study to Determine Eligibility for CAH-301 (A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH) [NCT04783181])

Congenital Adrenal Hyperplasia Clinical Trial

Official title:
Pre-screening Study to Identify Adult Participants With Classic Congenital Adrenal Hyperplasia Due to 21-Hydroxylase Deficiency Who May Be Eligible for Treatment in the CAH-301 Trial With BBP-631, an Adeno-associated Virus (AAV) Serotype 5-Based Recombinant Vector Encoding the Human CYP21A2 Gene

Clinical Trial Summary

This pre-screening study is designed to determine potential eligibility of adults with classic CAH due to 21-hydroxylase deficiency (21-OHD) for participation in the CAH-301 [NCT04783181] gene therapy trial with BBP-631.

Clinical Trial Description

Adult participants diagnosed with classic CAH due to 21-OHD and who are taking glucocorticoids as treatment for CAH will undergo assessments to determine their potential eligibility for participation in the adult CAH-301 treatment trial with BBP-631. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT05101902
Study type Observational
Source Adrenas Therapeutics Inc
Contact Patient Advocacy
Phone 650-391-9740
Email ClinicalTrials@AdrenasTX.com
Status Recruiting
Phase
Start date July 1, 2021
Completion date June 2024
View Details
See also
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