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Clinical Trial Summary

This is a single-arm, multi-site, single-dose, Phase 3 study in approximately 18 participants less than or equal to (<=) 50 years of age with transfusion-dependent β-thalassemia (TDT), who have a β0/β0, β0/IVS-I-110, or IVS-I-110/IVS-I-110 genotype. The study will evaluate the efficacy and safety of autologous hematopoietic stem cell transplantation (HSCT) using LentiGlobin BB305 Drug Product.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT03207009
Study type Interventional
Source bluebird bio
Contact
Status Completed
Phase Phase 3
Start date June 8, 2017
Completion date November 15, 2022

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