Natural History Study of Batten Disease

Status Terminated

Clinical Trial Summary

This is a multicenter, international, study to assess the natural history data from people with Batten disease by collecting both retrospective and prospective information about the motor, behavioral and functional capabilities of patients. The study initially has 2 cohorts. Cohort 1 (n ≈ 75) includes subjects with CLN6 Batten disease. Cohort 2 (n ≈ 120) includes subjects with juvenile CLN3 Batten disease. Additional cohorts for other Batten disease subtypes may be added in the future.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Batten Disease
Neuronal Ceroid Lipofuscinosis CLN3
Neuronal Ceroid Lipofuscinosis CLN6
Neuronal Ceroid-Lipofuscinoses

Clinical Trial Details

NCT number	NCT04644549
Study type	Observational
Source	Amicus Therapeutics
Contact
Status	Terminated
Phase
Start date	April 27, 2021
Completion date	March 11, 2022

View Details

See also
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