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Clinical Trial Summary

The purpose of this study is to evaluate the efficacy and safety of VX-864 in participants with the PiZZ genotype over 48 weeks.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT05643495
Study type Interventional
Source Vertex Pharmaceuticals Incorporated
Contact
Status Active, not recruiting
Phase Phase 2
Start date February 23, 2023
Completion date December 2024

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