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Clinical Trial Summary

This is a Phase 2, multicenter, open-label extension of Study DCR-A1AT-201, designed to evaluate the long-term safety and further characterize the pharmacodynamics (PD) of belcesiran in adult patients with PiZZ AATLD.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT05146882
Study type Interventional
Source Dicerna Pharmaceuticals, Inc.
Contact
Status Withdrawn
Phase Phase 2
Start date December 2021
Completion date May 23, 2022

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