MD1003-AMN MD1003 in Adrenomyeloneuropathy

Status Completed

Clinical Trial Summary

The primary objective of the trial is to demonstrate the superiority of biotin at 300 mg/day over placebo in the clinical improvement (walking tests) of patients with adrenomyeloneuropathy

Clinical Trial Description

AMN and progressive multiple sclerosis share some similarities including progressive spastic paraparesis and secondary energy failure leading to progressive axonal degeneration. Therefore, it was hypothesized that high doses of biotin might be efficient in patients with AMN. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT02961803
Study type	Interventional
Source	MedDay Pharmaceuticals SA
Contact
Status	Completed
Phase	Phase 2/Phase 3
Start date	October 2014
Completion date	June 2017

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