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Clinical Trial Summary

This is a Phase 2, open-label, sequential cohort dose-escalation study of BMN 111 in children with achondroplasia. The primary objective is to assess the safety and tolerability of daily BMN 111 administered to children with achondroplasia.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT02055157
Study type Interventional
Source BioMarin Pharmaceutical
Contact
Status Completed
Phase Phase 2
Start date January 13, 2014
Completion date October 2, 2017

See also
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