An Open Label Study to Evaluate the Pharmacokinetics, Safety, Tolerability and Efficacy of Deferasirox Administered to Chinese Patients With β-thalassemia Major Aged From 2 to Less Than 6 Years Old — MACS2163

ß-thalassemia Major Clinical Trial

Official title:
An Open Label Study to Evaluate the Pharmacokinetics, Safety, Tolerability and Efficacy of Deferasirox Administered to Chinese Patients With β-thalassemia Major Aged From 2 to Less Than 6 Years Old

Status Withdrawn

Clinical Trial Summary

To characterize the PK of deferasirox in pediatric β-thalassemia major patients aged from 2 to less than 6 years old, when administrated with a fixed starting dose of 20 mg/kg/day.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT01724138
Study type	Interventional
Source	Novartis
Contact
Status	Withdrawn
Phase	Phase 4
Start date	June 2013
Completion date	October 2014

View Details

See also
Status	Clinical Trial	Phase
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Terminated	`NCT04205435` - β-globin Restored Autologous HSC in β-thalassemia Major Patients	Phase 1/Phase 2
Not yet recruiting	`NCT04592458` - Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients	Phase 1
Completed	`NCT01745120` - A Study Evaluating the Safety and Efficacy of the LentiGlobin BB305 Drug Product in β-Thalassemia Major Participants	Phase 1/Phase 2
Recruiting	`NCT05776173` - Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent β-thalassemia	N/A