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A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects — INCEPTUS  

X-linked Myotubular Myopathy Clinical Trial

Official title:
INCEPTUS: A Prospective, Non-Interventional Clinical Assessment Study in X Linked Myotubular Myopathy (XLMTM) Subjects Aged 3 Years and Younger

Clinical Trial Summary

This is a pre-Phase 1 prospective, non interventional clinical assessment study to evaluate XLMTM subjects aged 3 years and younger. Many of these clinically relevant measures have not yet been routinely assessed in this population and may provide important insight on the natural history of XLMTM and for future evaluation of potential therapies.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT02704273
Study type Observational
Source Astellas Pharma Inc
Contact
Status Completed
Phase
Start date July 2016
Completion date September 2019
View Details
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Completed NCT01840657 - Myotubular Myopathy Event Study N/A