A Long-term Follow-up Study in Participants Who Received CTX001

Status Enrolling by invitation

Clinical Trial Summary

This is a multi-site, open- label rollover study to evaluate the long-term safety and efficacy of CTX001 in pediatric and adult participants who received CTX001 in parent studies 111 (NCT03655678) 141 (NCT05356195) or 161 (NCT05477563) (transfusion-dependent β-thalassemia [TDT] studies) or Study 121 (NCT03745287) or 151 (NCT05329649), 161(NCT05477563),171 (NCT05951205) (severe sickle cell disease [SCD] studies).

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT04208529
Study type	Interventional
Source	Vertex Pharmaceuticals Incorporated
Contact
Status	Enrolling by invitation
Phase	Phase 3
Start date	January 20, 2021
Completion date	September 2039

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See also
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