Safety & Efficacy of Gene Therapy of the Sickle Cell Disease by

Status Active, not recruiting

Clinical Trial Summary

The purpose of this study is to evaluate the Safety and Efficacy of Gene Therapy of the Sickle Cell disease by Transplantation of an Autologous CD34+ enriched cell fraction that contains CD34+ cells transduced ex vivo with the GLOBE1 lentiviral vector expressing the βAS3 globin gene (GLOBE1 βAS3 Modified Autologous CD34+ Cells) in Patients with Sickle Cell Disease (SCD)

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT03964792
Study type	Interventional
Source	Assistance Publique - Hôpitaux de Paris
Contact
Status	Active, not recruiting
Phase	Phase 1/Phase 2
Start date	November 12, 2019
Completion date	January 2024

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See also
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