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Expanded Access to Voxelotor for Patients With Sickle Cell Disease Who Have No Alternative Treatment Options

Sickle Cell Disease Clinical Trial

Official title:
An Open-Label, Expanded Access Protocol for Patients With Sickle Cell Disease Who Have No Alternative Treatment Options

Clinical Trial Summary

The intent of this open-label, multicenter expanded access program (EAP) is to provide early access to voxelotor prior to market authorization

Clinical Trial Description

The purpose of this program is to provide early access to voxelotor for patients with sickle cell disease who have exhausted alternative treatment options and are ineligible for actively-recruiting clinical trials of voxelotor. This EAP may continue until such time that voxelotor is commercially available or the Sponsor discontinues the voxelotor EAP. Discontinuation may occur earlier if an individual participant or physician or Sponsor Medical Monitor decides to discontinue treatment. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT03943615
Study type Expanded Access
Source Pfizer
Contact
Status No longer available
Phase
View Details
See also
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