|
Completed
|
NCT01942590 -
Safety and Efficacy of Clenbuterol in Individuals With Late-onset Pompe Disease and Receiving Enzyme Replacement Therapy
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Phase 1/Phase 2 |
|
Not yet recruiting
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NCT01409486 -
Screening for Early Detection and Prevention of Pompe Disease in Israel Using Tandem Mass Spectrometry
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N/A |
|
Completed
|
NCT00976352 -
Safety Study of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase to Treat Pompe Disease
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Phase 1/Phase 2 |
|
Recruiting
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NCT01665326 -
Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease
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|
|
Completed
|
NCT01758354 -
Newborn Screening Assay of Pompe's Disease
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N/A |
|
Recruiting
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NCT00231400 -
Pompe Disease Registry Protocol
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|
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Recruiting
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NCT05687474 -
Baby Detect : Genomic Newborn Screening
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|
|
Recruiting
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NCT04476550 -
Clinical Specimen Collection From Pompe Disease Patients
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|
|
Completed
|
NCT01380743 -
Drug-drug Interaction Study
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Phase 2 |
|
Recruiting
|
NCT05734521 -
Avalglucosidase Alfa Pregnancy Study
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|
|
Completed
|
NCT02742298 -
Pompe Disease QMUS and EIM
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N/A |
|
Terminated
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NCT02185651 -
A Pilot Study of Zavesca® in Patients With Pompe Disease and Infusion Associated Reaction
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Phase 1 |
|
Completed
|
NCT02654886 -
Safety and Effectiveness of Resistance Exercise Training in Patients With Pompe Disease.
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N/A |
|
Completed
|
NCT02405598 -
Evaluation of Salbutamol as an Adjuvant Therapy for Pompe Disease
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Phase 4 |
|
Completed
|
NCT00701129 -
An Exploratory Study of the Safety and Efficacy of Prophylactic Immunomodulatory Treatment in Myozyme-naive Cross-Reacting Immunologic Material (CRIM[-]) Patients With Infantile-Onset Pompe Disease
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Phase 4 |
|
Completed
|
NCT01451879 -
Observational Study for Subjects With Pompe Disease Undergoing Immune Modulation Therapies
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N/A |
|
Completed
|
NCT02240407 -
Re-administration of Intramuscular AAV9 in Patients With Late-Onset Pompe Disease
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Phase 1 |
|
Completed
|
NCT05073783 -
A Study to Assess the Safety of Myozyme® and of Aldurazyme® in Male and Female Participants of Any Age Group With Pompe Disease or With Mucopolysaccharidosis Type I (MPS I) in a Home-care Setting
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|
|
Active, not recruiting
|
NCT04093349 -
A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)
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Phase 1/Phase 2 |
|
Completed
|
NCT02363153 -
Diet and Exercise in Pompe Disease
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N/A |