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Clinical Trial Summary

Patients with infantile onset Pompe disease will be trained with continuous positive airway pressure to see if hypernasality can be improved.


Clinical Trial Description

n/a


Study Design

Endpoint Classification: Efficacy Study, Intervention Model: Single Group Assignment, Masking: Open Label, Primary Purpose: Treatment


Related Conditions & MeSH terms


NCT number NCT02405624
Study type Interventional
Source National Taiwan University Hospital
Contact Yin-Hsiu Chien
Phone 886223123456
Email chienyh@ntu.edu.tw
Status Recruiting
Phase Phase 4
Start date June 2014
Completion date June 2016

See also
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Completed NCT02363153 - Diet and Exercise in Pompe Disease N/A