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Clinical Trial Summary

This program is designed to provide access to pozelimab and cemdisiran and document the long-term safety of pozelimab and cemdisiran combination therapy in patients with paroxysmal nocturnal hemoglobinuria (PNH). PNH is a rare immune disease that causes red blood cells in your body to break apart.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT06028594
Study type Expanded Access
Source Regeneron Pharmaceuticals
Contact Requests for compassionate use must be initiated by a treating p
Phone +44(0) 1932 824 100
Email medicineaccess@clinigengroup.com
Status Available
Phase

See also
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