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Pediatric Spinal Muscular Atrophy (SMA) China Registry

Muscular Atrophy, Spinal Clinical Trial

Official title:
Pediatric Patients With Spinal Muscular Atrophy in China: A Nationwide Registry

Clinical Trial Summary

The primary objective of the study is to describe the natural history and utilization of disease modifying therapy (DMT) treatments among pediatric Chinese participants with spinal muscular atrophy linked to chromosome 5q (5q-SMA).

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT05042921
Study type Observational [Patient Registry]
Source Biogen
Contact US Biogen Clinical Trial Center
Phone 866-633-4636
Email clinicaltrials@biogen.com
Status Recruiting
Phase
Start date November 18, 2021
Completion date September 2, 2027
View Details
See also
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