A Study to Collect Blood Samples From Patients With Spinal Muscular

See also
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Recruiting	`NCT05755451` - Natural History of SMA
Active, not recruiting	`NCT01233817` - Progressive Strength Training in Spinal Muscular Atrophy	N/A
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Active, not recruiting	`NCT05618379` - Adult Spinal Muscular Atrophy (SMA) China Registry
Active, not recruiting	`NCT04488133` - A Study of Nusinersen Among Participants With Spinal Muscular Atrophy Who Received Onasemnogene Abeparvovec	Phase 4
Completed	`NCT03781479` - Controlled Trial to Evaluate Amifampridine Phosphate in Spinal Muscular Atrophy Type 3 Patients	Phase 2
Completed	`NCT00568698` - A Pilot Therapeutic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy Patients	Phase 1/Phase 2

NCT number	NCT01910168
Study type	Observational
Source	Hoffmann-La Roche
Contact
Status	Completed
Phase	N/A
Start date	August 2013
Completion date	February 2014

A Study to Collect Blood Samples From Patients With Spinal Muscular Atrophy for Biomarker Analysis

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms