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Clinical Trial Summary

This is a natural history study for children up to 18 years of age who have been diagnosed with Mucopolysaccharidosis Type IIIB (MPS IIIB, also known as Sanfilippo Syndrome Type B). Mucopolysaccharidosis type IIIB is a severe neurodegenerative disorder. The information gathered from this trial may help inform the design and interpretation of subsequent interventional studies. No clinical intervention or study drug is provided by Allievex in this study.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT03227042
Study type Observational
Source Allievex Corporation
Contact
Status Active, not recruiting
Phase
Start date November 16, 2017
Completion date December 2025

See also
  Status Clinical Trial Phase
Completed NCT02493998 - A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)
Completed NCT02037880 - Natural History Studies of Mucopolysaccharidosis III N/A
Active, not recruiting NCT03784287 - A Treatment Extension Study of Mucopolysaccharidosis Type IIIB Phase 2
Completed NCT02754076 - A Treatment Study of Mucopolysaccharidosis Type IIIB Phase 1/Phase 2