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Clinical Trial Summary

This multicenter, multinational, longitudinal study will quantify endurance and respiratory function in subjects diagnosed with MPS IVA and will better characterize the spectrum of symptoms and biochemical abnormalities in MPS IVA disease over time.


Clinical Trial Description

n/a


Study Design

Observational Model: Case-Only


Related Conditions & MeSH terms


NCT number NCT00787995
Study type Observational
Source BioMarin Pharmaceutical
Contact
Status Terminated
Phase N/A
Start date October 2008
Completion date July 2014

See also
  Status Clinical Trial Phase
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Completed NCT01515956 - Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome) Phase 2
Active, not recruiting NCT03632213 - Evaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VI Phase 2
Terminated NCT01242111 - A Study to Evaluate the Long-Term Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) Phase 1/Phase 2
Recruiting NCT05284006 - Non-invasive Functional Assessment and Pathogenesis of Morquio A
Completed NCT02208661 - Psychological Concomitants of Morquio A Syndrome - Longitudinal Effects of Enzyme Replacement Therapy (The MAPLE Study)
Completed NCT01415427 - Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) Phase 3
Terminated NCT01697319 - Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation Phase 2
Terminated NCT01609062 - Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome Phase 2
Approved for marketing NCT01858103 - BMN 110 US Expanded Access Program N/A