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Higher Dose of Alglucosidase Alpha for Pompe Disease

Glycogen Storage Disease Type II Clinical Trial

Official title:
Higher Dose of Alglucosidase Alpha for Pompe Disease: Long-term Follow-up Study

Clinical Trial Summary

This study is aimed to investigate that whether the higher dose ERT improve safety and clinical outcomes of Pompe disease patients. Also, wish to develop a new therapeutic recommendation and hope that it could improve the long-term outcomes of Pompe diesease patients.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT05017402
Study type Observational
Source Taipei Veterans General Hospital, Taiwan
Contact
Status Not yet recruiting
Phase
Start date September 1, 2021
Completion date December 31, 2026
View Details
See also
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