Higher Dose of Alglucosidase Alpha for Pompe Disease

See also
Status	Clinical Trial	Phase
Recruiting	`NCT00231400` - Pompe Disease Registry Protocol
Recruiting	`NCT04910776` - Clinical Study for Treatment-naïve IOPD Babies to Evaluate Efficacy and Safety of ERT With Avalglucosidase Alfa	Phase 3
Withdrawn	`NCT01656590` - High Protein and Exercise Therapy Plus Nocturnal Enteral Feeding in Juvenile-onset Pompe Disease	Phase 2
Completed	`NCT00701129` - An Exploratory Study of the Safety and Efficacy of Prophylactic Immunomodulatory Treatment in Myozyme-naive Cross-Reacting Immunologic Material (CRIM[-]) Patients With Infantile-Onset Pompe Disease	Phase 4
Active, not recruiting	`NCT04093349` - A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)	Phase 1/Phase 2
Completed	`NCT02363153` - Diet and Exercise in Pompe Disease	N/A
Completed	`NCT00074932` - Expanded Access Use of Myozyme (Alglucosidase Alfa) in Patients With Late-onset Pompe Disease	N/A
Completed	`NCT00025896` - Safety and Efficacy of Recombinant Human Acid Alpha-Glucosidase in the Treatment of Classical Infantile Pompe Disease	Phase 2
Completed	`NCT00001331` - Genetic and Family Studies of Inherited Muscle Diseases	N/A
Completed	`NCT00077662` - A Prospective, Observational Study in Patients With Late-Onset Pompe Disease	N/A
Recruiting	`NCT05951790` - Inspiratory Muscle Training (IMT) in Adult People With Pompe Disease	N/A
Completed	`NCT00125879` - Extension Study of Patients With Infantile-Onset Pompe Disease Who Were Previously Enrolled in Protocol AGLU01602	Phase 2/Phase 3
Recruiting	`NCT04848779` - A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients ≤6 Months of Age With Infantile-onset Pompe Disease (IOPD)
Active, not recruiting	`NCT05164055` - Avalglucosidase Alfa French Post-trial Access for Participants With Pompe Disease (PTA Avalglucosidase)	Phase 4
Recruiting	`NCT02761421` - Effect of Motor Development, Motor Function and Electrophysiologic Findings of IOPD Under ERT	N/A
Active, not recruiting	`NCT02635269` - Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy	N/A
Completed	`NCT00051935` - A Study of the Safety and Pharmacokinetics of rhGAA in Siblings With Glycogen Storage Disease Type II	Phase 2
Completed	`NCT00053573` - rhGAA in Patients With Infantile-onset Glycogen Storage Disease-II (Pompe Disease)	Phase 1/Phase 2
Completed	`NCT02801539` - Respiratory Muscle Training in L-Onset Pompe Disease (LOPD)	N/A
Completed	`NCT03687333` - Evaluate Efficacy and Safety in Chinese Patients With Infantile-Onset Pompe Disease With One Year Alglucosidase Alfa Treatment	Phase 4

NCT number	NCT05017402
Study type	Observational
Source	Taipei Veterans General Hospital, Taiwan
Contact
Status	Not yet recruiting
Phase
Start date	September 1, 2021
Completion date	December 31, 2026

Higher Dose of Alglucosidase Alpha for Pompe Disease

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms