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Clinical Trial Summary

Phase 1 Single Ascending Dose Study in Normal Healthy Volunteers


Clinical Trial Description

This is a study in humans of ELX-02, an advanced synthetic aminoglycoside optimized as a translational read-through drug (TRID) for the treatment of genetic conditions caused by nonsense mutations. This is a classical Phase 1a study designed as a randomized, double-blinded, placebo-controlled, single dose escalation to evaluate the safety, tolerability and pharmacokinetics of ELX-02 in healthy adult volunteers. ;


Study Design


Related Conditions & MeSH terms


NCT number NCT03292302
Study type Interventional
Source Eloxx Pharmaceuticals, Inc.
Contact
Status Completed
Phase Phase 1
Start date September 26, 2017
Completion date December 15, 2017

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