Beta-Thalassemia Clinical Trial
Official title:
A Safety and Effectiveness Registry Study of Patients With β-Thalassemia Treated With Betibeglogene Autotemcel (the Glostar Registry)
The main aim of this study is to collect real-world longitudinal data on participants with β-thalassemia treated with betibeglogene autotemcel (beti-cel) in the post marketing setting. To assess the long-term safety, including the risk of newly diagnosed malignancies, after treatment with beti-cel and evaluate the long-term effectiveness of treatment with beti-cel.
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| Status | Clinical Trial | Phase | |
|---|---|---|---|
| Completed |
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N/A | |
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Phase 1 |