Clinical trial NCT03955679 - References

Spinal Muscular Atrophy — AveXis Managed Access Program Cohort for Access to AVXS-101

Citation(s)

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A Managed Access Program (MAP) Cohort Treatment Protocol to Provide AVXS-101 to Patients With a Genetic Diagnosis of Spinal Muscular Atrophy (SMA) With 1, 2 or 3 Copies of SMN2

Details for clinical trial NCT03955679