Clinical trial NCT03538899 - References

Severe Combined Immunodeficiency — Autologous Gene Therapy for Artemis-Deficient SCID

Citation(s)

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A Phase I/II Feasibility Study of Gene Transfer for Artemis-Deficient Severe Combined Immunodeficiency (ART-SCID) Using a Self-Inactivating Lentiviral Vector (AProArt) to Transduce Autologous CD34 Hematopoietic Cells

Details for clinical trial NCT03538899